Precision gene editing could prevent vision loss from Stargardt disease
Researchers have developed a therapy to treat Stargardt disease, the most common form of inherited macular degeneration, ...
AZoLifeSciences on MSN5d
Breakthrough Gene Editing Technique Offers Hope for Stargardt Disease Patients
Rewriting genes to preserve eyesight IOB and Beam Therapeutics develop efficient gene editing technique for Stargardt disease ...
Pharmaceutical Technology28m
Insmed’s gene therapy for DMD poised to challenge landscape after IND clearance
Insmed is set to challenge the Duchenne muscular dystrophy (DMD) treatment space with its innovative gene therapy asset, INS1201.
Alkeus Pharmaceuticals to Present at the 43rd Annual J.P. Morgan Healthcare Conference
Inc., a biopharmaceutical company dedicated to preserving the sight of individuals impacted by retinal diseases, today ...
Medical Xpress5d
Precision gene editing could prevent vision loss from Stargardt disease
Stargardt disease affects around one in 6,500 people and is therefore a rare disease. Those affected increasingly lose the ability to see in the center of their field of vision, which makes it ...