Muscular Dystrophy News5d
Corticosteroid at low dose may help with muscle damage, inflammation
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
Muscular Dystrophy News3d
FDA awards fast track designation to DM1 treatment DYNE-101
The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...
Muscular Dystrophy News11d
DYNE-101 is leading to functional gains for DM1 patients in trial
DYNE-101 eased myotonia and led to other functional improvements for people with myotonic dystrophy type 1 (DM1) in a ...
Muscular Dystrophy News13d
GIVI-MPC named FDA orphan drug for treatment of Becker MD
GIVI-MPC, a stem cell therapy for certain types of muscular dystrophy, has been granted orphan drug status for treating ...
Muscular Dystrophy News3d
What success looks like for me as a DMD parent
Parenting is the most challenging job I’ve ever had. When my role as a parent expanded into caregiving for three of my children, challenging didn’t even begin to describe the path that lay in front of ...
Muscular Dystrophy News10d
Stuck in limbo with both accessible vans out of commission
An accident and a malfunction render both of columnist Betty Vertin's accessible vans useless, leaving the family without transportation.
Muscular Dystrophy News12d
How my FSHD progression leads to out-of-body experiences
Many times over the years since the 1989 car crash that nearly killed me, I’ve been asked if I had any near-death or out-of-body experiences while I hung between life and death. I always try to ...